Insecticides have been used for centuries to counteract widespread pest damage to valuable food crops. Eventually, over time, beetles, moths, flies ...

After years of setbacks, biotechs are advancing treatments for Huntington’s disease, offering new hope as clinical studies ...

US President-elect Donald Trump’s announcement of a proposed Department of Government Efficiency (DOGE) drew varied reactions ...

Neurobiology, Neurodegeneration and Repair Laboratory, National Eye Institute, National Institutes of Health, Bethesda, United States This important study employed multiple orthogonal techniques and ...

A new technology that delivers two halves of a gene separately could enable gene therapy treatments of muscular dystrophies.

StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.

CRISPR-Cas9 is a powerful gene-editing tool that allows scientists to modify DNA in living organisms precisely. It works like ...

Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is a big problem: size. The ...