SGT-212 is the company's novel, AAV-based FA gene therapy candidate designed to deliver full-length frataxin via systemic intravenous (IV) infusion as well as direct intradentate nuclei (IDN) infusion ...
In the PET trial, RAP-219 achieved and exceeded target receptor occupancy, increasing support for the dosing regimen utilized in the ongoing Phase 2a trial in focal epilepsy; restricted ...
By Mekado Murphy ‘The Room Next Door’ | Anatomy of a Scene Pedro Almodóvar narrates a sequence from his film starring Julianne Moore and Tilda Swinton. By Mekado Murphy ‘Wicked ...