“We expect a first data readout next year that seeks to confirm ATX-01’s mechanism of action.” ARTHEx also has ATX-01 in preclinical testing for myotonic dystrophy type 2 (DM2). “Although ...

Patients with myotonic dystrophy have smaller hearts, and lower systolic and diastolic blood pressures and pulse rates. They have impaired autonomic reflexes, measured by orthostatic, Valsalva ...

San Diego-based Kate is focused on preclinical programs aimed at Duchenne muscular dystrophy (DMD), facioscapulohumeral dystrophy (FSHD) and myotonic ... experiences of the first wave of companies ...