Many human diseases are multigenic, meaning they result from mutations in multiple genes. How are the complex traits of these diseases identified and treated? Of course, these patterns of gene ...

Penn researchers introduce mvGPT, a gene editing tool that edits DNA, activates genes and represses gene expression ...

It is also engaged in collaborative efforts to harmonize regulatory requirements across different countries and regions to streamline the approval of rare disease gene therapies and ensure access ...

Researchers have developed an AI model that accurately predicts gene activity in any human cell, providing insights into ...

Usher syndrome (USH) is a rare hereditary genetic disorder characterized by hearing loss, visual impairment, and balance dysfunction. Patients with USH have ...

A new predictive AI system has been developed to predict gene activity in human cells with high precision. Researchers at ...

Genome-wide inference of microRNA modulators identified a post-transcriptional regulatory network in GBM that was predictive of aberrant expression of GBM driver genes. MicroRNA modulators in the PCI ...

A multi-institutional team of researchers has created a new and improved genetic map for the laboratory rat, a cornerstone in ...

Alternative splicing is crucial for eukaryotic gene expression and influences protein function and regulation, with mis-splicing linked to numerous diseases. In this webinar, Dr. Megan L Noonan will ...

Azafaros B.V. today announced that its lead asset, nizubaglustat, has been granted orphan drug designation from regulatory authorities in both the United States and the European Union for the ...

New Delhi, Jan. 02, 2025 (GLOBE NEWSWIRE) -- The global gene therapy market was valued at US$ 9.42 billion in 2024 and is projected to hit the market valuation of US$ 42.26 billion by 2033 at a CAGR ...